Fatima Bosch
Company: Universitat Autònoma de Barcelona, Spain
Job title: Professor & Director, Center of Animal Biotechnology & Gene Therapy
Seminars:
Translational Gene Therapy Approaches to Treat Mucopolysaccharidosis 11:15 am
Discussing the potentiality of intracerebrospinal fluid adenoassociated viral (AAV) vector-mediated gene therapy to counteract neurologic and somatic MPS Using this approach to treat for MPSII and MPSIII, expression of the different therapeutic genes was detected in widespread brain regions and in the liver, leading to increased enzyme activity in CNS and serum and simultaneous correction…Read more
day: Day One